1. Preface
1.1. Report Scope and Market Segmentation
1.2. Research Highlights
2. Assumptions and Research Methodology
2.1. Assumptions and Acronyms Used
2.2. Research Methodology
3. Executive Summary
3.1. Global Gene Therapy Market Analysis, by Region, 2021 and 2031
3.2. Global Gene Therapy Market: Market Snapshot
4. Market Overview
4.1. Global Gene Therapy Market Overview
4.2. Global Gene Therapy Market Key Industry Developments
4.3. Market Dynamics
4.3.1. Drivers and Restraints Snapshot Analysis
4.3.2. Drivers
4.3.3. Restraints
4.3.4. Opportunities
4.4. Global Gene Therapy Market Analysis and Forecasts, 2021–2031
5. Key Insights
5.1. Regulatory Scenario by Region/globally
5.2. Clinical Trial Pipeline Analysis
5.3. Overview of Manufacturers
6. Global Gene Therapy Market Analysis, by Product
6.1. Introduction
6.2. Key Insights
6.3. Global Gene Therapy Market Application and Forecast, by Product
6.3.1. Yescarta
6.3.2. Kymriah
6.3.3. Luxturna
6.3.4. Strimvelis
6.3.5. Gendicine
6.4. Global Gene Therapy Market Analysis, by Product
6.5. Global Gene Therapy Market Attractiveness Analysis, by Product
7. Global Gene Therapy Market Analysis, by Application
7.1. Introduction
7.2. Key Insights
7.3. Global Gene Therapy Market Application and Forecast, by Application
7.3.1. Ophthalmology
7.3.2. Oncology
7.3.3. Adenosine DeaminaseDeficient Severe Combined Immunodeficiency (ADA-SCID)
7.4. Global Gene Therapy Market Analysis, by Application
7.5. Global Gene Therapy Market Attractiveness Analysis, by Application
8. Global Gene Therapy Market Analysis, by Region
8.1. Introduction
8.2. Key Insights
8.3. Global Gene Therapy Market Size and Forecast , by Region, 2016–2031
8.3.1. United States
8.3.2. Europe
8.3.3. Rest of World
8.4. Global Gene Therapy Market Analysis, by Region
8.5. Global Gene Therapy Market Attractiveness Analysis, by Region
9. United States Gene Therapy Market Analysis
9.1. United States Gene Therapy Market Key Findings
9.2. United States Gene Therapy Market Overview
9.3. United States Gene Therapy Market Size and Forecast, by Product
9.3.1. Yescarta
9.3.2. Kymriah
9.3.3. Luxturna
9.3.4. Strimvelis
9.3.5. Gendicine
9.4. United States Gene Therapy Market Application and Forecast, by Application
9.4.1. Ophthalmology
9.4.2. Oncology
9.4.3. Adenosine DeaminaseDeficient Severe Combined Immunodeficiency (ADA-SCID)
9.5. United States Gene Therapy Market Attractiveness Analysis
9.5.1. By Product
9.5.2. By Application
9.5.3. By Country
10. Europe Gene Therapy Market Analysis
10.1. Europe Gene Therapy Market Key Findings
10.2. Europe Gene Therapy Market Overview
10.3. Europe Gene Therapy Market Size and Forecast, by Product
10.3.1. Yescarta
10.3.2. Kymriah
10.3.3. Luxturna
10.3.4. Strimvelis
10.3.5. Gendicine
10.4. Europe Gene Therapy Market Size and Forecast, by Application
10.4.1. Ophthalmology
10.4.2. Oncology
10.4.3. Adenosine DeaminaseDeficient Severe Combined Immunodeficiency (ADA-SCID)
10.5. Europe Gene Therapy Market Forecast, by Country
10.5.1. Germany
10.5.2. U.K.
10.5.3. France
10.5.4. Spain
10.5.5. Italy
10.5.6. Rest of Europe
10.6. Europe Gene Therapy Market Attractiveness Analysis
10.6.1. By Product
10.6.2. By Application
10.6.3. By Country
11. Rest of World Gene Therapy Market Analysis
11.1. Rest of World Gene Therapy Market Key Findings
11.2. Rest of World Gene Therapy Market Overview
11.3. Rest of World Gene Therapy Market Size and Forecast, by Product
11.3.1. Yescarta
11.3.2. Kymriah
11.3.3. Luxturna
11.3.4. Strimvelis
11.3.5. Gendicine
11.4. Rest of World Gene Therapy Market Size and Forecast, by Application
11.4.1. Ophthalmology
11.4.2. Oncology
11.4.3. Adenosine DeaminaseDeficient Severe Combined Immunodeficiency (ADA-SCID)
11.5. Rest of World Gene Therapy Market Attractiveness Analysis
11.5.1. By Product
11.5.2. By Application
11.5.3. By Country
12. Competition Landscape
12.1. Global Gene Therapy Market Share Analysis, by Company (2016)
12.2. Company Profiles
12.2.1. Novartis AG
12.2.1.1. Overview (HQ, Employee Strength, Business Segments)
12.2.1.2. Financials
12.2.1.3. Recent Developments
12.2.1.4. Strategy
12.2.2. Orchard Therapeutics Limited.
12.2.2.1. Overview (HQ, Employee Strength, Business Segments)
12.2.2.2. Financials
12.2.2.3. Recent Developments
12.2.2.4. Strategy
12.2.3. CELGENE CORPORATION
12.2.3.1. Overview (HQ, Employee Strength, Business Segments)
12.2.3.2. Financials
12.2.3.3. Recent Developments
12.2.3.4. Strategy
12.2.4. Spark Therapeutics, Inc.
12.2.4.1. Overview (HQ, Employee Strength, Business Segments)
12.2.4.2. Financials
12.2.4.3. Recent Developments
12.2.4.4. Strategy
12.2.5. Gilead Sciences, Inc.
12.2.5.1. Overview (HQ, Employee Strength, Business Segments)
12.2.5.2. Financials
12.2.5.3. Recent Developments
12.2.5.4. Strategy
12.2.6. Sibiono GeneTech Co. Ltd.
12.2.6.1. Overview (HQ, Employee Strength, Business Segments)
12.2.6.2. Financials
12.2.6.3. Recent Developments
12.2.6.4. Strategy
Table 1: Pipeline Analysis: Gene therapy Candidates (1/8)Table 2: Pipeline Analysis: Gene therapy Candidates (2/8)
Table 3: Pipeline Analysis: Gene therapy Candidates (3/8)
Table 4: Pipeline Analysis: Gene therapy Candidates (4/8)
Table 5: Pipeline Analysis: Gene therapy Candidates (5/8)
Table 6: Pipeline Analysis: Gene therapy Candidates (6/8)
Table 7: Pipeline Analysis: Gene therapy Candidates (7/8)
Table 8: Pipeline Analysis: Gene therapy Candidates (8/8)
Table 9: Global Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 10: Global Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 11: Global Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 12: Global Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 13: U.S. Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 14: U.S. Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 15: U.S. Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 16: U.S. Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 17: Europe Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 18: Europe Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 19: Europe Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 20: Europe Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 21: Rest of the World Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 22: Rest of the World Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 23: Rest of the World Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 24: Rest of the World Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 25: Germany Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 26: Germany Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 27: Germany Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 28: Germany Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 29: France Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 30: France Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 31: France Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 32: France Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 33: Italy Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 34: Italy Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 35: Italy Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 36: Italy Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 37: Spain Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 38: Spain Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 39: Spain Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 40: Spain Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 41: U.K. Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2016–2020
Table 42: U.K. Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2016–2020
Table 43: U.K. Gene Therapy Market Size (US$ Mn) Forecast, by Product, 2021–2031
Table 44: U.K. Gene Therapy Market Size (US$ Mn) Forecast, by Application, 2021–2031
Table 45: Germany Gene Therapy Market Size (US$ Mn), 2021-2031
Table 46: France Gene Therapy Market Size (US$ Mn), 2021-2031
Table 47: Italy Gene Therapy Market Size (US$ Mn), 2021-2031
Table 48: Spain Gene Therapy Market Size (US$ Mn), 2021-2031
Table 49: U.K. Gene Therapy Market Size (US$ Mn), 2021-2031
Table 50: Germany Gene Therapy Market Y-O-Y Analysis, 2021-2031
Table 51: France Gene Therapy Market Y-O-Y Analysis, 2021-2031
Table 52: Italy Gene Therapy Market Y-O-Y Analysis, 2021-2031
Table 53: Spain Gene Therapy Market Y-O-Y Analysis, 2021-2031
Table 54: U.K. Gene Therapy Market Y-O-Y Analysis, 2021-2031
Table 55: Germany Gene Therapy Market Share Analysis, 2021-2031
Table 56: France Gene Therapy Market Share Analysis, 2021-2031
Table 57: Italy Gene Therapy Market Share Analysis, 2021-2031
Table 58: Spain Gene Therapy Market Share Analysis, 2021-2031
Table 59: U.K. Gene Therapy Market Share Analysis, 2021-2031
Figure 01: Market Segmentation: Global Gene Therapy Market
Figure 02: Research Methodology: Global Gene Therapy Market
Figure 03: Analysis by Product
Figure 04: Analysis by Application
Figure 05: Analysis by Region
Figure 06: Key Industry Developments
Figure 07: Drivers and Restraints: Global Gene Therapy Market
Figure 08: Global Gene Therapy Market Value (US$ Mn) Forecast, 2021–2031
Figure 09: Global Gene Therapy Market Value Share, by Product (2016)
Figure 10: Global Gene Therapy Market Value Share, by Application (2016)
Figure 11: Global Gene Therapy Market Value Share, by Country/Region (2016)
Figure 12: Key Findings: Global Gene Therapy Market, by Product
Figure 13: Introduction: Global Gene Therapy Market, by Product
Figure 14: Global Gene Therapy Market Value Share Analysis, by Product, 2021 and 2031
Figure 15: Global Gene Therapy Market Attractiveness Analysis, by Product, 2021–2031
Figure 16: Global Gene Therapy Market Revenue (US$ Mn), by Yescarta, 2021–2031
Figure 17: Global Gene Therapy Market Revenue (US$ Mn), by Kymriah, 2021–2031
Figure 18: Global Gene Therapy Market Revenue (US$ Mn), by Luxturna, 2021–2031
Figure 19: Global Gene Therapy Market Revenue (US$ Mn), by Strimvelis, 2021–2031
Figure 20: Global Gene Therapy Market Revenue (US$ Mn), by Gendicine, 2021–2031
Figure 21: Key Findings: Global Gene Therapy Market, by Application
Figure 22: Introduction: Global Gene Therapy Market, by Application
Figure 23: Global Gene Therapy Market Value Share Analysis, by Application, 2021 and 2031
Figure 24: Global Gene Therapy Market Attractiveness Analysis, by Product, 2021–2031
Figure 25: Global Gene Therapy Market Revenue (US$ Mn ), by Ophthalmology, 2021–2031
Figure 26: Global Gene Therapy Market Revenue (US$ Mn), by Oncology, 2021–2031
Figure 27: Global Gene Therapy Market Revenue (US$ Mn ), by ADA-SCID, 2021–2031
Figure 28: U.S. Gene Therapy Market Size (U.S.$ Mn) and Y-o-Y Growth (%) Forecast, 2021–2031
Figure 29: U.S. Gene Therapy Market Value Share Analysis, by Product, 2021 and 2031
Figure 30: U.S. Gene Therapy Market Value Share Analysis, by Product, 2021 and 2031
Figure 31: U.S. Gene Therapy Market Value Share Analysis, by Application, 2021 and 2031
Figure 32: U.S. Gene Therapy Market Attractiveness Analysis, by Application, 2021–2031
Figure 33: Europe Gene Therapy Market Size (US$ Mn) and Y-o-Y Growth (%) Forecast, 2021–2031
Figure 34: Europe Gene Therapy Market Value Share Analysis, by Product, 2021 and 2031
Figure 35: Europe Gene Therapy Market Attractiveness Analysis, by Product, 2021-2031
Figure 36: Europe Gene Therapy Market Value Share Analysis, by Application, 2021 and 2031
Figure 37: Europe Gene Therapy Market Attractiveness Analysis, by Application, 2021–2031
Figure 38: Rest of the World Gene Therapy Market Size (US$ Mn) and Y-o-Y Growth (%) Forecast, 2021–2031
Figure 39: Rest of the World Gene Therapy Market Value Share Analysis, by Product, 2021 and 2031
Figure 40: Rest of the World Gene Therapy Market Attractiveness Analysis, by Product, 2021-2031
Figure 41: Rest of the World Gene Therapy Market Value Share Analysis, by Application, 2021 and 2031
Figure 42: Rest of the World Gene Therapy Market Attractiveness Analysis, by Application, 2021–2031
Figure 43: Competition Matrix: Global Gene Therapy Market
Figure 44: Novartis AG, Company Details
Figure 45: Novartis AG, Product Portfolio
Figure 46: Novartis AG, Breakdown of Net Sales, by Geography (2016)
Figure 47: Novartis AG, Breakdown of Net Sales, by Business Segment (2016)
Figure 48: Novartis AG, Revenue (US$ Bn) & Y-o-Y Growth (%), 2016–2016
Figure 49: Novartis AG, R&D Intensity and Sales & Marketing Intensity – Company Level, 2017–2016
Figure 50: Novartis AG, SWOT Analysis
Figure 51: Orchard Therapeutics Limited, Company Details
Figure 52: Orchard Therapeutics Limited, Product Portfolio
Figure 53: Orchard Therapeutics Limited, SWOT Analysis
Figure 54: CELGENE CORPORATION, Company Details
Figure 55: CELGENE CORPORATION, Product Portfolio
Figure 56: CELGENE CORPORATION, Revenue (US$ Bn) & Y-o-Y Growth (%), 2017–2020
Figure 57: CELGENE CORPORATION, Breakdown of Net Sales, by Key Products (2016)
Figure 58: CELGENE CORPORATION, Breakdown of Net Sales, by Geography (2016)
Figure 59: CELGENE CORPORATION, R&D Intensity and Sales & Marketing Intensity: Company Level, 2016-2017
Figure 60: CELGENE CORPORATION, SWOT Analysis
Figure 61: Spark Therapeutics, Inc., Company Details
Figure 62: Spark Therapeutics, Inc., Product Portfolio
Figure 63: Spark Therapeutics, Inc., Revenue (US$ Mn) & Y-o-Y Growth (%), 2016–2020
Figure 64: Spark Therapeutics, Inc., R&D Expenditure, 2017–2016
Figure 65: Spark Therapeutics, Inc., SWOT Analysis
Figure 66: Gilead Sciences, Inc., Company Details
Figure 67: Gilead Sciences, Inc., Product Portfolio
Figure 68: Gilead Sciences, Inc., Revenue (US$ Bn) & Y-o-Y Growth (%), 2016–2020
Figure 69: Gilead Sciences, Inc., R&D Expenditure (US$ Bn), 2016–2020
Figure 70: Gilead Sciences, Inc., SWOT Analysis
Figure 71: Sibiono GeneTech Co. Ltd, Company Details
Figure 72: Sibiono GeneTech Co. Ltd., Product Portfolio
Figure 73: Sibiono GeneTech Co. Ltd., SWOT Analysis
Figure 74: U.S. Gene Therapy Market Absolute $ Opportunity, 2021-2031
Figure 75: Germany Gene Therapy Market Absolute $ Opportunity, 2021-2031
Figure 76: France Gene Therapy Market Absolute $ Opportunity, 2021-2031
Figure 77: Italy Gene Therapy Market Absolute $ Opportunity, 2021-2031
Figure 78: Spain Gene Therapy Market Absolute $ Opportunity, 2021-2031
Figure 79: U.K. Gene Therapy Market Absolute $ Opportunity, 2021-2031